www.dpm.tn
Direction de la Pharmacie et du Médicament (National Drug Administration) in Tunisia

www.pct.tn
Central Pharmacy of Tunisia (Pharmacie Centrale de Tunisie)

www.orpha.net
Database for rare and orphan diseases and their treatments

www.eurordis.org
European organization for rare diseases. A federation of patients associations and influencers in the field of rare disorders.

FDA
U.S. Food and Drug Administration

EMEA
European Drug Agency (Agence Européenne du Médicament)

www.afssaps.sante.gouv
French Sanitary Security Agency for Health Products (Agence Française de Sécurité Sanitaire des Produits de Santé)

Public Summaries of Opinions for Orphan designation

European Agencies
National drug agencies from European countries


Répertoire des Spécialités Pharmaceutiques AFSSAPS

Directory of Pharmaceutical Specialties managed by the French Sanitary Security Agency

SFOPH
Swiss Federal Office for Public Health

SwissMedic (formally IOCM)
Swiss Medical Agency

Vml
Vaincre les Maladies Lysosomales Association (Association Against Lysosomal Diseases)

Fabrysuisse
Association for Fabry Disease Patients in Switzerland

Portail Officiel du Ministère de la Santé, de la Population et de la Réforme Hospitalière (Algérie)

Official portal of the Algerian Ministry of Health, Population and Hospital Reform

Companies deeply involved in Orphan Drugs

www. biomarin pharm.com

www.genzyme.com

www.shire.com (ex Transkaryotic Therapies)

www.orphan-europe.com

   
Copyright 2005 CarthaGenetics.