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Links
www.dpm.tn
Direction de la Pharmacie et du Médicament (National Drug Administration) in Tunisia
www.pct.tn
Central Pharmacy of Tunisia (Pharmacie Centrale de Tunisie)
www.orpha.net
Database for rare and orphan diseases and their treatments
www.eurordis.org
European organization for rare diseases. A federation of patients associations and influencers in the field of rare disorders.
FDA
U.S. Food and Drug Administration
EMEA
European Drug Agency (Agence Européenne du Médicament)
www.afssaps.sante.gouv
French Sanitary Security Agency for Health Products (Agence Française de Sécurité Sanitaire des Produits de Santé)
Public Summaries of Opinions for Orphan designation
European Agencies
National drug agencies from European countries
Répertoire des Spécialités Pharmaceutiques AFSSAPS
Directory of Pharmaceutical Specialties managed by the French Sanitary Security Agency
SFOPH
Swiss Federal Office for Public Health
SwissMedic (formally IOCM)
Swiss Medical Agency
Vml
Vaincre les Maladies Lysosomales Association (Association Against Lysosomal Diseases)
Fabrysuisse
Association for Fabry Disease Patients in Switzerland
Portail Officiel du Ministère de la Santé, de la Population et de la Réforme Hospitalière (Algérie)
Official portal of the Algerian Ministry of Health, Population and Hospital Reform
Companies deeply involved in Orphan Drugs
www. biomarin pharm.com
www.genzyme.com
www.shire.com (ex Transkaryotic Therapies)
www.orphan-europe.com
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